Expansion Therapeutics

Transformative oral medicines for severe RNA-mediated diseases.

About

Founded

2016

Headquarters

San Diego, California

Industry

Healthcare

Company Description

Expansion Therapeutics is a drug discovery and development company pursuing the vast potential of small molecule medicines for RNA-mediated diseases. Expansion has assembled the intellectual property, know-how, and proprietary enabling technologies and tools necessary to facilitate the creation of potent and specific small molecule binders of RNA. Through this unique platform, Expansion is building a portfolio of novel RNA-targeted drug candidates with activity across a broad number of disease indications. The company’s initial development focus is on therapies for patients with expansion repeat diseases who currently have limited and unsatisfactory treatment options.

Quick Links

WebsiteJobs

Funding

Total Raised

$142.2 million

Valuation

Undisclosed

Significant Investors

Westlake Village BioPartners, Surveyor Capital, Logos Capital, RA Capital Management, 5AM Ventures, Kleiner Perkins, Sanofi Ventures, Novartis Venture Fund

Company Traction

  • As of June 2023, Expansion Therapeutics has completed the discovery phase before pre-clinical trials for Myotonic Dystrophy Type 1, Amyotrophic Lateral Sclerosis (ALS) and Frontotemporal Dementia (FTD), and Dementias and Movement Disorders.

Leadership Team

  • Renato Skerlj: CEO at Expansion Therapeutics. Founder of X4 Pharmaceuticals.
  • Valerie Cullen: SVP of Research at Expansion Therapeutics. Former VP of Translation and Development at Generian.
  • Mark Ledeboer: SVP of Drug Discovery at Expansion Therapeutics. Former VP of Drug Discovery at Goldfinch Bio.
  • Jennifer Visco: VP of Finance & Business Operations at Expansion Therapeutics. Former Finance Director at Harvard Medical School.
  • Andrew Good: VP of Computational Chemistry at Expansion Therapeutics. Former Senior Director CADD and Cheminformatics at C4 Therapeutics.

People also viewed